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Overview of rare diseases worldwide and in the U.S. as of 2016
Overview of rare diseases worldwide and in the U.S. as of 2016
Number of rare diseases, disease patients and treatments worldwide and in the U.S. as of 2016
by Statista Research Department,
last edited
Feb 28, 2016
This statistic shows the number of known rare diseases, patients, and treatments worldwide and in the U.S. as of 2016. As of that time there were around 7,000 known rare diseases that affected 30 million people in the U.S. and 350 million people worldwide.
Number of rare diseases, disease patients and treatments worldwide and in the U.S. as of 2016
| Number | |
|---|---|
| Known rare diseases | 7,000 |
| U.S. Americans with rare diseases | 30,000,000 |
| People worldwide with rare diseases | 350,000,000 |
| Approved therapeutic treatments* | 400 |
| Number | |
|---|---|
| Known rare diseases | 7,000 |
| U.S. Americans with rare diseases | 30,000,000 |
| People worldwide with rare diseases | 350,000,000 |
| Approved therapeutic treatments* | 400 |
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by Statista Research Department,
last edited
Feb 28, 2016
This statistic shows the number of known rare diseases, patients, and treatments worldwide and in the U.S. as of 2016. As of that time there were around 7,000 known rare diseases that affected 30 million people in the U.S. and 350 million people worldwide.
- Show sources information
- Show publisher information
- Release date
- February 2016
- Region
- Worldwide, United States
- Survey time period
- as of 2016
- Supplementary notes
- * Approximate
Source
- Show sources information
- Show publisher information
- Release date
- February 2016
More information
- Region
- Worldwide, United States
- Survey time period
- as of 2016
- Supplementary notes
- * Approximate
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Statistics on "Orphan drugs"
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The most important statistics
- Global prescription orphan drug sales from 2010 to 2024 (in billion U.S. dollars)Projection of global revenue for orphan prescription drugs 2010-2024
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- Per-year list price of the top ten most expensive drugs worldwide as of 2018*Price comparison of the 10 most expensive drugs as of 2018
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- Top 50 global pharmaceutical companies by prescription sales and R&D spending in 2018 (in billion U.S. dollars)Top 50 pharmaceutical companies - Rx sales and R&D spending 2018
- Top pharmaceutical companies by orphan drug revenue worldwide in 2018 (in billion U.S. dollars)Top global companies by orphan drug revenues 2018
- Forecast of top 10 pharmaceutical companies by global orphan drug revenue in 2024 (in billion U.S. dollars)*Top 10 companies by global revenue from orphan drugs 2024
- Top 20 pharmaceutical companies worldwide by orphan drug revenue market share in 2024 compared to 2018*Market share of top 20 companies for orphan drugs worldwide 2018 and 2024
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The most important statistics
- Top global orphan drugs by revenue in 2018 (in billion U.S. dollars)*Top global orphan drugs by revenue 2018
- Projected top 10 orphan drugs worldwide by revenue in 2024 (in billion U.S. dollars)*Projection of top 10 orphan drugs by global revenue 2024
- Annual number of accepted orphan designations in the United States from 2003 to 2018Number of orphan designations accepted in the U.S. 2003-2018
- Percentage of select orphan drugs' U.S. revenues attributable to non-orphan usage in 2017Percentage of select orphan drug US sales by non/orphan use 2017
- Percentage of FDA-approved orphan drugs with additional non-orphan indications between 1983 and 2018FDA approved orphan drugs with non-orphan indications 1983-2018
- Research and development
The most important statistics
- Total global spending on pharmaceutical research and development from 2010 to 2024 (in billion U.S. dollars)Total global pharmaceutical R&D spending 2010-2024
- Projection of top 10 orphan drugs in development (phase III/filed) by NPV as of 2019 (in billion U.S. dollars)Leading orphan drugs in development based on net present value 2019
- Number of non-oncology orphan designated products currently being developed worldwide by company type as of April 2019Global therapeutic pipeline for non-oncology orphan drug programs by company 2019
- Average time from orphan drug designation to last remaining exclusivity in the U.S. as of 2018, by current statusTime from orphan drug design to final exclusivity 2018, by current status
- Probability of success for new rare disease and high prevalence disease drugs in the U.S. by development phase from 2006 to 2015U.S. development Phase success rates for rare and common disease drugs 2006-2015
- Rare diseases
The most important statistics
- Number of rare diseases, disease patients and treatments worldwide and in the U.S. as of 2016Overview of rare diseases worldwide and in the U.S. as of 2016
- Life expectancy for individuals with select rare diseases before available treatment and now worldwide as of 2017Impact of medicines on life expectancy for select rare diseases worldwide as of 2017
- Distribution of patients in the U.S. with rare factor deficiencies as of 2018, by gender* Distribution of U.S. patients with rare factor deficiencies as of 2018, by gender
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Statistics on "Orphan drugs"
- Projection of global revenue for orphan prescription drugs 2010-2024
- Annual growth in global revenue for prescribed orphan drugs 2011-2024
- Annual average cost of orphan drugs per patient 2014-2018
- Price comparison of the 10 most expensive drugs as of 2018
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- Number of orphan designations accepted in the U.S. 2003-2018
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- Total global pharmaceutical R&D spending 2010-2024
- Leading orphan drugs in development based on net present value 2019
- Global therapeutic pipeline for non-oncology orphan drug programs by company 2019
- Time from orphan drug design to final exclusivity 2018, by current status
- U.S. development Phase success rates for rare and common disease drugs 2006-2015
- Overview of rare diseases worldwide and in the U.S. as of 2016
- Impact of medicines on life expectancy for select rare diseases worldwide as of 2017
- Distribution of U.S. patients with rare factor deficiencies as of 2018, by gender
- U.S. rare disease patient feelings as of 2015
- Comorbidity in primary Sjögren's patients in the U.S. and EU 2015
- Share of primary Sjögren patients in the U.S. and EU using healthcare resources 2013
- Children in the U.S. with pneumococcal syndrome before immunization 2009
- Share of primary Sjögren's patients in the U.S. and EU with impairments 2011-2013
- Diagnosed autoimmune conditions by country and gender share 2018
- Total rare diseases funding by the National Institutes for Health 2013-2020
- Italy: rare disease patients treated within clinical trials 2017, by disease
- Peru: reported Dengue fever cases 2007-2019
- Brazil: number of cases of Dengue fever 2017-2018, by state
- Brazil: cities with the highest number of cases of Chikungunya in 2018
- Brazil: number of deaths due to Chikungunya virus 2017-2018
- Italy: value of rare disease projects funded by the Telethon Foundation 2011-2017
- Italy: number of rare disease projects funded by the Telethon Foundation 2012-2016
- Brazil: number of cases of Chikungunya 2017-2018, by state
- Brazil: number of deaths due to Chikungunya virus 2018, by region
- Number of whooping cough cases in Sweden 2018, by age group
- Brazil: number of cases of Chikungunya 2017-2018, by region
- Brazil: number of cases of Dengue fever 2018, by city
- Number of rabid cats and dogs in the U.S. from 2010 to 2015
- Italy: number of rubella cases 2017-2018, by month
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