Orphan drugs

The Statista dossier
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Statista dossier about the orphan drugs industry and market

Table of contents

    • Prevalence of selected rare diseases worldwide 2017

    • Overview of rare diseases worldwide and in the U.S. as of 2016

    • Impact of medicines on life expectancy for select rare diseases worldwide as of 2017

    • Distribution of U.S. patients with rare factor deficiencies as of 2021, by gender

    • Projection of global revenue for orphan prescription drugs 2012-2026

    • Annual growth in global revenue for prescribed orphan drugs 2011-2024

    • Price comparison of most expensive drugs U.S. 2021

    • Annual average cost of orphan drugs per patient 2014-2018

    • Global cell and gene therapy market share by therapy class 2019 & 2025

    • Global rare disease diagnostics market size 2018 vs. 2025 projection

    • Top 50 pharmaceutical companies - Rx sales and R&D spending 2021

    • Top global companies by orphan drug revenues 2018

    • Top 10 companies by global revenue from orphan drugs 2024

    • Market share of top 20 companies for orphan drugs worldwide 2018 and 2024

    • US and European private VC-backed orphan biopharma company M&A values 2014-2019

    • Top global orphan drugs by revenue 2018

    • Projection of top 10 orphan drugs by global revenue 2024

    • Number of orphan designations accepted in the U.S. 2003-2020

    • Oncology or orphan drug share in approved new active substances 2015-2020

    • FDA approved orphan drugs with non-orphan indications 1983-2018

    • Percentage of select orphan drug US sales by non/orphan use 2017

    • Total global pharmaceutical R&D spending 2012-2026

    • Total rare diseases funding by the National Institutes for Health 2013-2022

    • Leading orphan drugs in development based on net present value 2020

    • Global therapeutic pipeline for non-oncology orphan drug programs by company 2019

    • Time from orphan drug design to final exclusivity 2018, by current status

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